The BRAVE Study is evaluating a potential treatment option for Friedreich Ataxia.
If your child has been diagnosed with Friedreich Ataxia (FA), they may be eligible for the BRAVE Study.
The BRAVE Study is evaluating how safe a study drug is and how well it works for the treatment of Friedreich Ataxia (FA) for children aged 2–15.
The study drug is an oral capsule and will be compared to a placebo. A placebo looks just like the study drug but does not contain any active ingredients. Your child will be randomly assigned to take either the study drug or placebo once daily.
Your child will have a higher chance of receiving the study drug than the placebo. Neither you, your child, nor the study team will know which treatment they have been assigned to, but in case of an emergency, the study team can quickly find out.
NOTE: The study drug (investigational or placebo) may be taken as a capsule OR its contents sprinkled over certain foods, like applesauce, to make dosing easier.
Check now to see if your child may qualify!
Study Design
The BRAVE Study may last up to three years and is made up of two parts.
If your child completes Part 1 of the study, they may be able to enter Part 2. All participants in Part 2 will receive the study drug, even if they received the placebo in Part 1.
Take the next step to see if your child may qualify for the BRAVE Study.
Study Cost
Neither you nor your insurance provider will be charged for the costs of any tests or procedures performed as part of the clinical study. Travel support may be available if needed.
What you should know about clinical research studies
Regulations and policies have been developed to help protect the rights, safety, and well-being of people who take part in clinical research studies and to help ensure that these studies are conducted according to strict scientific and ethical principles. Before a clinical research study can begin, an institutional review board (IRB) or ethics committee (EC) must review and approve the study.
Participation in any clinical research study is completely voluntary, and you or your child may withdraw from a clinical research study at any time for any reason. Before participating in a clinical research study, it is important to weigh the potential risks and benefits of participation. The study team will inform you of the potential risks and benefits of study participation, as well as possible side effects. To make an informed decision, gather as much information as possible and talk to your or your child’s healthcare providers about any questions you may have.
During the study, you will work with a study team that may include study doctors, study nurses, and other research staff.
Thank you for considering the BRAVE Study.
What’s required to get started?
1. Answer some questions about your child’s health
2. Tell us a little bit about you/your child
3. Connect to an available study in your area
Just takes a few minutes
*In this research study, the participants may receive investigational study product or may receive an inactive substance, or placebo, depending on the study design.
Participants receive study-related care from a doctor/research team for the duration of the study. The length of the study may vary.